Gene Therapy Clinical Trial: Promising Results For Pompe Disease

Gene Therapy Clinical Trial: Promising Results for Pompe Disease

Gene Therapy and Pompe Disease: Preliminary Results From Phase I/II Study With AT845

New ERT for Pompe Disease Showing Promise

The Treatment of Pompe Disease: Clinical Updates in Newborn Screening and Enzyme Replacement

Pompe Disease and Gene Therapy

Enzyme Replacement Therapy Versus Gene Therapy

Gene Therapy for Fabry Disease Showing Promise

The Latest Developments in Pompe Disease Research

How Duke University Has Led Pompe Disease Research

Clinical Viewpoint on Newly Approved Combination Therapy for Pompe Disease

Gene Therapy and Pompe Disease

Rare Disease Report

Positive Results for First Gene Therapy Trial for Glycogen Storage Disease

Lentiviral Gene Therapy for Pompe Disease

AMDA YouTube Channel

Astellas Gene Therapies Webinar: Evaluating gene therapies for Pompe disease

AMDA YouTube Channel

Amicus releases phase 3 results in Pompe disease trial

CNBC Television

Patient Living with Pompe Disease and Participant in the COMET Clinical Trial

HPR

Realizing the Promise of Gene Therapy in Pompe | Progress in Halting Pompe Disease

Pompe Disease Explained

Genetics of Pompe Disease

MDA